Key highlights
Explore more by category
Showing: 1 – 10 of 45 stories
31 May 2023 – 1 mins read
Caitlin: learning to accept care as a caregiver
In September 2012, when she was 21, Caitlin received news every child dreads: her father had been diagnosed with pancreatic cancer and had been given three months to live.
23 May 2023 – 1 mins read
Fireside Chat: Innovation and Policy Change in Rare Diseases in Europe
The rare disease community continues to strive for innovative solutions to meet patient needs and ensure no person living with a rare disease is left behind.
23 May 2023 – 2 mins read
Applications now open for the 2023 Golden Ticket Competition
As part of our commitment to accelerating transformative research and development, we’re excited to announce that our Golden Ticket Competition is now open! Through our continued partnership with Biolabs, we’re delighted to be offering the brightest mi
12 May 2023 – 4 mins read
Understanding the true impact of living with FOP
This year marks the 17th anniversary since the discovery of the ACVR1 gene was announced, a major scientific milestone in fibrodysplasia ossificans progressiva (FOP) research that helped us understand what causes the condition. On April 23,
02 March 2023 – 1 mins read
Rethinking risk factors this Liver Cancer Awareness Month
Learn how to engage with our campaign and help protect your liver health. Every year, Liver Cancer Awareness Month (LCAM) is an opportunity to bring the sixth most prevalent cancer globally to the forefront of conversation, promoting awareness and the impo