{"id":64,"date":"2025-02-04T06:54:01","date_gmt":"2025-02-04T04:54:01","guid":{"rendered":"https:\/\/www.ipsen.com\/br\/?page_id=64"},"modified":"2025-07-31T13:28:13","modified_gmt":"2025-07-31T11:28:13","slug":"doencas-raras","status":"publish","type":"page","link":"https:\/\/www.ipsen.com\/brazil\/doencas-raras\/","title":{"rendered":"Doen\u00e7as Raras"},"content":{"rendered":"    <section class=\"sub-page-banner bg-img\" style=\"background-image:url(https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/06\/Health-Rare-Disease.jpg)\">\n        <div class=\"container content-sec\">\n            <nav aria-label=\"breadcrumb\">\n            <ol class=\"breadcrumb\">\n                <li class=\"breadcrumb-item\"><a href=\"https:\/\/www.ipsen.com\/brazil\">Home<\/a><\/li><li class=\"breadcrumb-item active\"><a href=\"#\" aria-current=\"page\">Ci\u00eancia &#8211; Doen\u00e7as Raras<\/a><\/li><\/ol>\n            <\/nav>            <h1 class=\"visible\">Doen\u00e7as Raras<\/h1>\n            <p class=\"visible\">Desenvolvendo op\u00e7\u00f5es de tratamento para pessoas com doen\u00e7as raras e ultrarraras<\/p>\n        <\/div>\n    <\/section>\n\n\n<!-- Ipsen Content Overlay Start -->\n<section class=\"two-col-image-section\">\n    <div class=\"container two-img-section-innner\"  >\n        <div class=\"content-overlay-inner bg-color-enabled\" style=\"background-color:#EDEBE4\">\n                <!-- Ipsen Content Overlay Variation Two Start -->\n                <div class=\"row \">\n                    <div class=\"col-xs-12 col-sm-12 col-md-6 column-1 \">\n                        <div id=\"image-carousel\" class=\"img-video-section carousel\" data-bs-ride=\"carousel\">\n                            <div class=\"carousel-inner\">\n                                                                        <div class=\"carousel-item active\">\n                                            <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/05\/Our-Commitment-to-Rare-Disease_Savannah_card-700x420pix.jpg\" alt=\"Media Image\" >\n                                        <\/div>\n                                                            <\/div>\n                                                    <\/div>\n                    <\/div>\n                    <div class=\" col-xs-12 col-sm-12 col-md-6 column-2 \">\n                        <div class=\" section-content\">\n                                                                <div class=\"heading-dash\">\n                                        <span class=\"dash\"><\/span>\n                                        <h4 role=\"heading\" aria-level=\"2\" class=\"heading-para-right heading-four\">\n                                            Nosso compromisso com doen\u00e7as raras                                        <\/h4>\n                                    <\/div>\n                                                                                                                        <p class=\"section-para \">\n                                        Doen\u00e7as Raras impactam 1 a cada 10 pessoas. Na Ipsen, nossas equipes est\u00e3o cada vez mais comprometidas em melhorar e prolongar a vida dessas pessoas. Somos dedicados ao desenvolvimento de novas e transformadoras op\u00e7\u00f5es de tratamento. Usamos nossa expertise cient\u00edfica para desenvolver medicamentos com potencial de mudar vidas, porque queremos estar presentes por aqueles que muitas vezes s\u00e3o deixados para tr\u00e1s.                                    <\/p>\n                                                                                <\/div>\n                    <\/div>\n                    <!-- Ipsen Content Overlay Variation Two End -->\n                <\/div>\n        <!-- Ipsen Content Overlay Variation two End -->\n                <\/div>\n    <\/div>\n<\/section>\n<!-- Ipsen Content Overlay End -->\n\n<!-- Text & Media Block Code -->\n<section class=\"two-col-section text-media-section\">\n    <div class=\"container two-section-innner section-reverse\">\n        <div class=\"response-inner\" style=\"background-image: url('')\">\n            <div class=\"row section-reverse\">\n                <div class=\"col-xs-12 col-sm-12 col-md-6\">\n                                                    <div class=\"img-video-section\">\n                                <img decoding=\"async\" \n                                    src=\"https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/07\/rare-1.jpg\" \n                                    alt=\"\" \n                                >\n                            <\/div>\n                                        <\/div>\n                <div class=\" col-xs-12 col-sm-12 col-md-6\">\n                    <div class=\"section-content\">\n                        <div class=\"heading-dash\">\n                                                            <span class=\"dash\"><\/span>\n                                <h4 class=\"heading-para heading-four\" role=\"heading\" aria-level=\"2\">\n                                    N\u00f3s somos a Ipsen em Doen\u00e7as Raras                                <\/h4>\n                                                    <\/div>\n                                                <p>Focamos nossas pesquisas e inova\u00e7\u00e3o nas \u00e1reas de maior necessidade n\u00e3o atendida e onde podemos gerar um impacto significativo para os pacientes. Nossa prioridade \u00e9 o avan\u00e7o de medicamentos e do conhecimento cient\u00edfico em doen\u00e7as raras e ultrarraras do f\u00edgado e dos ossos.<\/p>\n                            <a \n                            aria-label=\" about N\u00f3s somos a Ipsen em Doen\u00e7as Raras\"  \n                                role=\"link\" \n                                class=\"btn-link hidden\"\n                                href=\"\" \n                                target=\"_self\"\n                            > \n                                 \n                            <\/a>\n\n                    <\/div>\n                <\/div>\n            <\/div>\n        <\/div>\n    <\/div>\n<\/section>\n\n<!-- Ipsen Content Overlay Start -->\n<section class=\"two-col-image-section\">\n    <div class=\"container two-img-section-innner\"  >\n        <div class=\"content-overlay-inner bg-color-enabled\" style=\"background-color:#EDEBE4\">\n                <!-- Ipsen Content Overlay Variation Two Start -->\n                <div class=\"row \">\n                    <div class=\"col-xs-12 col-sm-12 col-md-6 column-1 \">\n                        <div id=\"image-carousel\" class=\"img-video-section carousel\" data-bs-ride=\"carousel\">\n                            <div class=\"carousel-inner\">\n                                                                        <div class=\"carousel-item active\">\n                                            <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/07\/05-04_PATIENTS_Text-and-Photos-Overlapped_Nadine-FOP-img-05-HD_NADINE.jpg\" alt=\"Media Image\" >\n                                        <\/div>\n                                                            <\/div>\n                                                    <\/div>\n                    <\/div>\n                    <div class=\" col-xs-12 col-sm-12 col-md-6 column-2 \">\n                        <div class=\" section-content\">\n                                                                <div class=\"heading-dash\">\n                                        <span class=\"dash\"><\/span>\n                                        <h4 role=\"heading\" aria-level=\"2\" class=\"heading-para-right heading-four\">\n                                            O compromisso inabal\u00e1vel da Ipsen com os pacientes                                        <\/h4>\n                                    <\/div>\n                                                                                                                        <p class=\"section-para \">\n                                        Pessoas que vivem com uma doen\u00e7a rara enfrentam barreiras di\u00e1rias, incluindo diagn\u00f3sticos tardios e tratamentos atrasados ou inadequados. A natureza cr\u00f4nica, progressiva, degenerativa e frequentemente limitadora da vida de muitas doen\u00e7as raras pode ter um impacto profundo na qualidade de vida. Estamos comprometidos em apoiar os pacientes desde o diagn\u00f3stico at\u00e9 o tratamento, e em colaborar com a comunidade para proporcionar melhores resultados para todos.                                    <\/p>\n                                                                                <\/div>\n                    <\/div>\n                    <!-- Ipsen Content Overlay Variation Two End -->\n                <\/div>\n        <!-- Ipsen Content Overlay Variation two End -->\n                <\/div>\n    <\/div>\n<\/section>\n<!-- Ipsen Content Overlay End -->\n\n<!-- Ipsen Content Overlay Start -->\n<section class=\"two-col-image-section\">\n    <div class=\"container two-img-section-innner\"  >\n        <div class=\"content-overlay-inner bg-color-enabled\" style=\"background-color:#EDEBE4\">\n                <!-- Ipsen Content Overlay Variation Two Start -->\n                <div class=\"row section-bg-reverse\">\n                    <div class=\"col-xs-12 col-sm-12 col-md-6 column-1 order-2\">\n                        <div id=\"image-carousel\" class=\"img-video-section carousel\" data-bs-ride=\"carousel\">\n                            <div class=\"carousel-inner\">\n                                                                        <div class=\"carousel-item active\">\n                                            <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/07\/Image16-1.jpg\" alt=\"Media Image\" >\n                                        <\/div>\n                                                            <\/div>\n                                                    <\/div>\n                    <\/div>\n                    <div class=\" col-xs-12 col-sm-12 col-md-6 column-2 order-1\">\n                        <div class=\" section-content\">\n                                                                <div class=\"heading-dash\">\n                                        <span class=\"dash\"><\/span>\n                                        <h4 role=\"heading\" aria-level=\"2\" class=\"heading-para-right heading-four\">\n                                            Nosso foco em ci\u00eancia                                        <\/h4>\n                                    <\/div>\n                                                                                                                        <p class=\"section-para \">\n                                        Um dos maiores desafios nas doen\u00e7as raras \u00e9 a limitada pesquisa cient\u00edfica e o conhecimento dispon\u00edvel para orientar nossa compreens\u00e3o. Iniciamos programas de desenvolvimento cl\u00ednico que ampliam o entendimento cient\u00edfico sobre as doen\u00e7as raras e seu impacto, com o objetivo de abrir caminho para uma melhor gest\u00e3o dessas doen\u00e7as e futuros avan\u00e7os terap\u00eauticos.                                    <\/p>\n                                                                                <\/div>\n                    <\/div>\n                    <!-- Ipsen Content Overlay Variation Two End -->\n                <\/div>\n        <!-- Ipsen Content Overlay Variation two End -->\n                <\/div>\n    <\/div>\n<\/section>\n<!-- Ipsen Content Overlay End -->\n\n<!-- Ipsen Content Overlay Start -->\n<section class=\"two-col-image-section\">\n    <div class=\"container two-img-section-innner\"  >\n        <div class=\"content-overlay-inner bg-color-enabled\" style=\"background-color:#EDEBE4\">\n                <!-- Ipsen Content Overlay Variation Two Start -->\n                <div class=\"row \">\n                    <div class=\"col-xs-12 col-sm-12 col-md-6 column-1 \">\n                        <div id=\"image-carousel\" class=\"img-video-section carousel\" data-bs-ride=\"carousel\">\n                            <div class=\"carousel-inner\">\n                                                                        <div class=\"carousel-item active\">\n                                            <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/06\/Science-with-Purpose.png\" alt=\"Media Image\" >\n                                        <\/div>\n                                                            <\/div>\n                                                    <\/div>\n                    <\/div>\n                    <div class=\" col-xs-12 col-sm-12 col-md-6 column-2 \">\n                        <div class=\" section-content\">\n                                                                <div class=\"heading-dash\">\n                                        <span class=\"dash\"><\/span>\n                                        <h4 role=\"heading\" aria-level=\"2\" class=\"heading-para-right heading-four\">\n                                            Nosso foco em inova\u00e7\u00e3o                                        <\/h4>\n                                    <\/div>\n                                                                                                                        <p class=\"section-para \">\n                                        Nossa miss\u00e3o \u00e9 reduzir a dist\u00e2ncia entre a ci\u00eancia inovadora e a melhora da sa\u00fade dos pacientes. Estamos focados em novas op\u00e7\u00f5es de tratamento que atendam \u00e0s necessidades reais de m\u00e9dicos e pacientes, e estamos investindo nosso tempo e recursos na pesquisa de medicamentos que atuem de forma diferente \u2014 com potencial transformador para alterar ou retardar o curso de uma doen\u00e7a e aliviar a dor e o sofrimento causados por sintomas debilitantes.                                    <\/p>\n                                                                                <\/div>\n                    <\/div>\n                    <!-- Ipsen Content Overlay Variation Two End -->\n                <\/div>\n        <!-- Ipsen Content Overlay Variation two End -->\n                <\/div>\n    <\/div>\n<\/section>\n<!-- Ipsen Content Overlay End -->\n\n    <section class=\"title-text \">\n        <div class=\"container\">\n            <div class=\"title-text-inner\" style=\"background-color:#EDEBE4;\">\n\n                <!-- If heading is enabled then it's visible -->\n                <div class=\"text-head-dash visible\">\n                <h3 class=\"heading-three\" role=\"heading\" aria-level=\"2\">\n                        Doen\u00e7as Raras do f\u00edgado                    <\/h3>\n                <\/div>\n               \n                <!-- If description is enabled then it's visible -->\n                <div class=\"text-parbase visible\">\n                    <p>As doen\u00e7as hep\u00e1ticas colest\u00e1ticas raras englobam um grupo de condi\u00e7\u00f5es pouco frequentes que afetam os ductos biliares, causando doen\u00e7as hep\u00e1ticas progressivas e sintomas como coceira persistente e fadiga. Esses sintomas podem ser extremamente debilitantes, mas muitas vezes s\u00e3o invis\u00edveis e mal compreendidos. A maioria das doen\u00e7as hep\u00e1ticas colest\u00e1ticas raras possui tratamentos aprovados bastante limitados. Devido \u00e0 sua raridade, os pacientes enfrentam in\u00fameros desafios no dia a dia. A jornada at\u00e9 o diagn\u00f3stico pode ser longa e tortuosa. Os pacientes frequentemente se sentem isolados e n\u00e3o ouvidos. \u00c0s vezes, sentem-se estigmatizados e incompreendidos. A necessidade de inova\u00e7\u00e3o \u00e9 enorme.<\/p>\n<p>N\u00f3s levamos medicamentos transformadores \u00e0s pessoas que vivem com doen\u00e7as hep\u00e1ticas raras. Realizamos essa ambi\u00e7\u00e3o enquanto mantemos o foco no crescimento cont\u00ednuo e na expans\u00e3o do nosso pipeline l\u00edder na ind\u00fastria em f\u00edgado raro. Iniciamos o desenvolvimento de nossos medicamentos ouvindo as pessoas que s\u00e3o especialistas em conviver com sua condi\u00e7\u00e3o, as fam\u00edlias que as apoiam e os profissionais de sa\u00fade com experi\u00eancia no tratamento das doen\u00e7as hep\u00e1ticas colest\u00e1ticas raras. Somente ouvindo \u00e9 que podemos garantir que os verdadeiros desafios da doen\u00e7a sejam compreendidos e representados no desenho de nossos ensaios cl\u00ednicos, nas iniciativas de conscientiza\u00e7\u00e3o e nos programas de suporte ao paciente.<\/p>\n                <\/div>\n\n                <!-- If button is enabled then it's visible -->\n                \n            <\/div>\n        <\/div>\n    <\/section>\n\n\n<!--Graphics Cards Carousel Start Here-->\n\n    <section class=\"graphic-card graphics-old-layout bg-color-disabled bg-image-disabled bg-video-disabled bg-mobile-video-img-disabled\"    data-displaycards=\"2\">\n                <div class=\"container\">\n            <div class=\"text-graph-inner\">\n                <div class=\"row\">\n                    <!--Graphic info section-->\n                    <div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n                        <div class=\"text-graph-heading\">\n                        <h3 class=\"charcoal-grey hidden heading-three\" role=\"heading\" aria-level=\"2\">\n                                                            <\/h3>\n                            <p class=\"text-graph-para charcoal-grey hidden\"><\/p>\n                        <\/div>\n                    <\/div><!--Graphic info section over here -->\n\n                    <!--Graphic detail section-->\n                    <div class=\"column-2 col-xl-12 col-md-12 col-sm-12\">\n                        <!-- graphic-card carousel start here -->\n                                                    <div class=\"text-graph-carousel\">\n                                <div class=\"glider-contain multiple\">\n                                    \n                                <div class=\"glider-graphic-card\" tabindex=\"-1\">\n                                                                                                                        <div class=\"text-graphic\">\n                                                    <div class=\"text-graph-row\">\n                                                        \n                                                                <!-- Graphic Card With OLD layout start here -->\n                                                                <div class=\"column-1\">\n                                                                                                                                                <div class=\"text-graph-img visible graphic-icon-enabled \">\n                                                                                                                                                                    <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/05\/Rare-Disease-Common.png\" alt=\"\" \/> \n                                                                                                                                                            <\/div>\n                                                                                                                                    <\/div>\n                                                                <div class=\"column-2\">\n                                                                    <div class=\"text-graph-content\">\n                                                                                                                                                        <div class=\"text-graph-title\">\n                                                                                <h4 role=\"heading\" aria-level=\"3\">O impacto das doen\u00e7as raras do f\u00edgado<\/h4>\n                                                                                <\/div>\n                                                                                                                                                <div class=\"text-graph-desc\">\n                                                                            <p><p>As doen\u00e7as raras do f\u00edgado s\u00e3o mais comuns do que se imagina, afetando cerca de 1 em cada 50.000 a 100.000 pessoas.<\/p>\n<\/p>\n                                                                        <\/div>\n                                                                    <\/div>\n                                                                <\/div>\n                                                                <!-- Graphic Card With OLD layout end here -->\n                                                        \n                                                    <\/div>\n                                                <\/div>\n                                                                                                                <\/div>\n                            <\/div>\n                                            <\/div> <!-- graphic-card carousel end here -->\n                <\/div> <!--Graphic detail section over here with 12 grid -->   \n            <\/div><!--row ended here-->\n        <\/div> <!-- graph-inner ended here -->\n        \n            <div class=\"more-result-btn\">\n                                            <\/div>\n        <\/div> <!--Container class ended here -->\n    <\/section>\n<!--Graphics Cards Carousel End Here-->\n\n\n\n    <!--Accordion Cards Start Here-->\n    <section class=\"accordion bg-color-disabled\"  data-according-id=\"1563908577\">\n        <div class=\"container\">\n            <div class=\"row\">\n                <!--Accordion info section-->\n                <div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n                    <div class=\"accordian-info\">\n                        <h3 class=\"accordian-heading visible heading-three\" role=\"heading\" aria-level=\"2\">\n                            Doen\u00e7as raras do f\u00edgado                        <\/h3>\n                        <p class=\"accordian-summary hidden\"><\/p>\n                    <\/div>\n                <\/div><!--Accordion info section over here -->\n\n                <div class=\"col-xl-12 col-lg-12 col-md-12 col-sm-12\">\n                    <div class=\"accordion accor-group\" id=\"accordionExample1563908577\">\n                         \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading0\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading15639085770\" aria-expanded=\"false\" aria-controls=\"expHeading15639085770\">\n                                                Colangite biliar prim\u00e1ria (CBP)                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading15639085770\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading0\" data-bs-parent=\"#accordionExample1563908577\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><p>A CBP (Colangite Biliar Prim\u00e1ria) \u00e9 uma doen\u00e7a hep\u00e1tica rara, autoimune, colest\u00e1tica e progressiva, em que o ac\u00famulo de bile e toxinas (colestase), junto com a inflama\u00e7\u00e3o cr\u00f4nica, causa fibrose (cicatrizes) irrevers\u00edvel no f\u00edgado e destrui\u00e7\u00e3o dos ductos biliares.<\/p>\n<p>A CBP afeta principalmente mulheres entre 40 e 60 anos.<\/p>\n<p>\u00c9 uma condi\u00e7\u00e3o cr\u00f4nica que pode piorar ao longo do tempo se n\u00e3o for tratada de forma eficaz, podendo levar ao transplante de f\u00edgado e, em alguns casos, \u00e0 morte precoce.<\/p>\n<p>A CBP impacta a vida cotidiana, com as pessoas frequentemente enfrentando sintomas de fadiga intensa e coceira persistente (prurido).<\/p>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                             \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading1\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading15639085771\" aria-expanded=\"false\" aria-controls=\"expHeading15639085771\">\n                                                Colestase intra-hep\u00e1tica familiar progressiva (PFIC)                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading15639085771\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading1\" data-bs-parent=\"#accordionExample1563908577\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><p>A PFIC refere-se a um grupo de doen\u00e7as gen\u00e9ticas raras em que o f\u00edgado tem dificuldade em drenar os \u00e1cidos biliares, causando o ac\u00famulo de bile no f\u00edgado \u2014 condi\u00e7\u00e3o conhecida como colestase intra-hep\u00e1tica.<\/p>\n<p>Embora a PFIC possa se manifestar na idade adulta, geralmente aparece e se apresenta de forma mais agressiva em beb\u00eas e crian\u00e7as pequenas.<\/p>\n<p>A PFIC pode progredir rapidamente, levando \u00e0 cirrose (cicatriza\u00e7\u00e3o hep\u00e1tica de longo prazo).<\/p>\n<p>O sintoma mais debilitante da PFIC \u00e9 o prurido (coceira persistente), que pode ser t\u00e3o severo a ponto de causar les\u00f5es na pele, perda de sono, irritabilidade, dificuldade de concentra\u00e7\u00e3o e baixo desempenho escolar.<\/p>\n<p>At\u00e9 80% dos pacientes sofrem com prurido.<\/p>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                             \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading2\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading15639085772\" aria-expanded=\"false\" aria-controls=\"expHeading15639085772\">\n                                                S\u00edndrome de Alagille (ALGS)                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading15639085772\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading2\" data-bs-parent=\"#accordionExample1563908577\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><p>A s\u00edndrome de Alagille (ALGS) \u00e9 uma doen\u00e7a hep\u00e1tica gen\u00e9tica e rara que afeta principalmente beb\u00eas e crian\u00e7as pequenas, caracterizada pelo ac\u00famulo de \u00e1cidos biliares t\u00f3xicos devido \u00e0 presen\u00e7a de ductos biliares em menor n\u00famero que o normal, estreitados ou malformados.<\/p>\n<p>A ALGS pode afetar diversos \u00f3rg\u00e3os do corpo, incluindo f\u00edgado, cora\u00e7\u00e3o e rins, al\u00e9m de causar anormalidades na pele, no esqueleto e nos olhos.<\/p>\n<p>Um dos principais sintomas \u00e9 o prurido intrat\u00e1vel (coceira persistente), que pode ser t\u00e3o severo a ponto de levar \u00e0 necessidade de um transplante de f\u00edgado.<\/p>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                                                <\/div>\n                <\/div> \n            <\/div>\n        <\/div>\n    <\/section>\n    <!--Accordion Cards End Here-->\n\n\n    <section class=\"title-text \">\n        <div class=\"container\">\n            <div class=\"title-text-inner\" style=\"background-color:#EDEBE4;\">\n\n                <!-- If heading is enabled then it's visible -->\n                <div class=\"text-head-dash visible\">\n                <h3 class=\"heading-three\" role=\"heading\" aria-level=\"2\">\n                        Dist\u00farbios end\u00f3crinos do crescimento                    <\/h3>\n                <\/div>\n               \n                <!-- If description is enabled then it's visible -->\n                <div class=\"text-parbase visible\">\n                    <p>Os dist\u00farbios do crescimento s\u00e3o causados quando o corpo produz horm\u00f4nio do crescimento em excesso ou em quantidade insuficiente. Isso pode fazer com que crian\u00e7as e adultos apresentem um crescimento anormal dos ossos e das cartilagens, como ocorre na acromegalia. Por outro lado, crian\u00e7as e adolescentes podem ter seu potencial de crescimento comprometido, n\u00e3o atingindo a estatura esperada.<\/p>\n                <\/div>\n\n                <!-- If button is enabled then it's visible -->\n                \n            <\/div>\n        <\/div>\n    <\/section>\n\n\n\n    <!--Accordion Cards Start Here-->\n    <section class=\"accordion bg-color-disabled\"  data-according-id=\"703158817\">\n        <div class=\"container\">\n            <div class=\"row\">\n                <!--Accordion info section-->\n                <div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n                    <div class=\"accordian-info\">\n                        <h3 class=\"accordian-heading visible heading-three\" role=\"heading\" aria-level=\"2\">\n                            Dist\u00farbios end\u00f3crinos do crescimento                        <\/h3>\n                        <p class=\"accordian-summary hidden\"><\/p>\n                    <\/div>\n                <\/div><!--Accordion info section over here -->\n\n                <div class=\"col-xl-12 col-lg-12 col-md-12 col-sm-12\">\n                    <div class=\"accordion accor-group\" id=\"accordionExample703158817\">\n                         \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading0\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading7031588170\" aria-expanded=\"false\" aria-controls=\"expHeading7031588170\">\n                                                Acromegalia                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading7031588170\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading0\" data-bs-parent=\"#accordionExample703158817\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><p>Acromegalia \u00e9 um dist\u00farbio raro causado por um tumor benigno (n\u00e3o cancer\u00edgeno) da gl\u00e2ndula hip\u00f3fise, chamado adenoma, que estimula a libera\u00e7\u00e3o excessiva do horm\u00f4nio do crescimento (GH) na corrente sangu\u00ednea. Como consequ\u00eancia, o corpo passa a produzir em maior quantidade outro horm\u00f4nio chamado fator de crescimento semelhante \u00e0 insulina tipo 1 (IGF-1).<\/p>\n<p>&nbsp;<\/p>\n<p>O excesso de IGF-1 e GH no organismo pode provocar crescimento anormal dos ossos, das cartilagens e de outros tecidos do corpo.<\/p>\n<p>&nbsp;<\/p>\n<p>Embora os sinais mais vis\u00edveis sejam o aumento das m\u00e3os, dos p\u00e9s e do rosto, problemas mais graves tamb\u00e9m podem se desenvolver.<\/p>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                                                <\/div>\n                <\/div> \n            <\/div>\n        <\/div>\n    <\/section>\n    <!--Accordion Cards End Here-->\n\n\n<!--Graphics Cards Carousel Start Here-->\n\n    <section class=\"graphic-card graphics-old-layout bg-color-disabled bg-image-disabled bg-video-disabled bg-mobile-video-img-disabled\"    data-displaycards=\"2\">\n                <div class=\"container\">\n            <div class=\"text-graph-inner\">\n                <div class=\"row\">\n                    <!--Graphic info section-->\n                    <div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n                        <div class=\"text-graph-heading\">\n                        <h3 class=\"charcoal-grey hidden heading-three\" role=\"heading\" aria-level=\"2\">\n                                                            <\/h3>\n                            <p class=\"text-graph-para charcoal-grey hidden\"><\/p>\n                        <\/div>\n                    <\/div><!--Graphic info section over here -->\n\n                    <!--Graphic detail section-->\n                    <div class=\"column-2 col-xl-12 col-md-12 col-sm-12\">\n                        <!-- graphic-card carousel start here -->\n                                                    <div class=\"text-graph-carousel\">\n                                <div class=\"glider-contain multiple\">\n                                                                                    <div class=\"text-graph-content-btn\">\n                                                    <button aria-hidden=\"true\" aria-label=\"Anterior\" class=\"glider-graphic-card-prev\"><span><\/span><\/button>\n                                                    <button aria-hidden=\"true\" aria-label=\"Pr\u00f3ximo\" class=\"glider-graphic-card-next\"><span><\/span><\/button>\n                                                <\/div>\n                                    \n                                <div class=\"glider-graphic-card\" tabindex=\"-1\">\n                                                                                                                        <div class=\"text-graphic\">\n                                                    <div class=\"text-graph-row\">\n                                                        \n                                                                <!-- Graphic Card With OLD layout start here -->\n                                                                <div class=\"column-1\">\n                                                                                                                                                <div class=\"text-graph-img visible graphic-icon-enabled \">\n                                                                                                                                                                    <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/05\/Document-1.png\" alt=\"\" \/> \n                                                                                                                                                            <\/div>\n                                                                                                                                    <\/div>\n                                                                <div class=\"column-2\">\n                                                                    <div class=\"text-graph-content\">\n                                                                                                                                                        <div class=\"text-graph-title\">\n                                                                                <h4 role=\"heading\" aria-level=\"3\">Informa\u00e7\u00e3o ao paciente<\/h4>\n                                                                                <\/div>\n                                                                                                                                                <div class=\"text-graph-desc\">\n                                                                            <p><p>Existem v\u00e1rios tipos de dist\u00farbios end\u00f3crinos do crescimento, incluindo a acromegalia. Esses dist\u00farbios podem impactar significativamente o crescimento e o desenvolvimento, e muitas vezes exigem interven\u00e7\u00e3o m\u00e9dica para controlar os n\u00edveis hormonais de forma eficaz.<\/p>\n<\/p>\n                                                                        <\/div>\n                                                                    <\/div>\n                                                                <\/div>\n                                                                <!-- Graphic Card With OLD layout end here -->\n                                                        \n                                                    <\/div>\n                                                <\/div>\n                                                                                                                                                                    <div class=\"text-graphic\">\n                                                    <div class=\"text-graph-row\">\n                                                        \n                                                                <!-- Graphic Card With OLD layout start here -->\n                                                                <div class=\"column-1\">\n                                                                                                                                                <div class=\"text-graph-img visible graphic-icon-enabled \">\n                                                                                                                                                                    <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/07\/Person.png\" alt=\"\" \/> \n                                                                                                                                                            <\/div>\n                                                                                                                                    <\/div>\n                                                                <div class=\"column-2\">\n                                                                    <div class=\"text-graph-content\">\n                                                                                                                                                        <div class=\"text-graph-title\">\n                                                                                <h4 role=\"heading\" aria-level=\"3\">Impacto na qualidade de vida<\/h4>\n                                                                                <\/div>\n                                                                                                                                                <div class=\"text-graph-desc\">\n                                                                            <p><p>Em compara\u00e7\u00e3o com crian\u00e7as de estatura normal, a baixa estatura pode impactar a qualidade de vida das crian\u00e7as e esse impacto pode persistir at\u00e9 a vida adulta.<\/p>\n<\/p>\n                                                                        <\/div>\n                                                                    <\/div>\n                                                                <\/div>\n                                                                <!-- Graphic Card With OLD layout end here -->\n                                                        \n                                                    <\/div>\n                                                <\/div>\n                                                                                                                                                                    <div class=\"text-graphic\">\n                                                    <div class=\"text-graph-row\">\n                                                        \n                                                                <!-- Graphic Card With OLD layout start here -->\n                                                                <div class=\"column-1\">\n                                                                                                                                                <div class=\"text-graph-img visible graphic-icon-enabled \">\n                                                                                                                                                                    <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/brazil\/wp-content\/uploads\/sites\/22\/2025\/07\/Psychosocial-Difficulties.png\" alt=\"\" \/> \n                                                                                                                                                            <\/div>\n                                                                                                                                    <\/div>\n                                                                <div class=\"column-2\">\n                                                                    <div class=\"text-graph-content\">\n                                                                                                                                                        <div class=\"text-graph-title\">\n                                                                                <h4 role=\"heading\" aria-level=\"3\">Dificuldades psicossociais<\/h4>\n                                                                                <\/div>\n                                                                                                                                                <div class=\"text-graph-desc\">\n                                                                            <p><p>Na vida adulta, pessoas que vivem com dist\u00farbios end\u00f3crinos do crescimento podem enfrentar dificuldades psicossociais, como piores perspectivas de emprego e condi\u00e7\u00f5es econ\u00f4micas desfavor\u00e1veis.<\/p>\n<\/p>\n                                                                        <\/div>\n                                                                    <\/div>\n                                                                <\/div>\n                                                                <!-- Graphic Card With OLD layout end here -->\n                                                        \n                                                    <\/div>\n                                                <\/div>\n                                                                                                                <\/div>\n                            <\/div>\n                                            <\/div> <!-- graphic-card carousel end here -->\n                <\/div> 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