{"id":43,"date":"2024-03-08T11:15:12","date_gmt":"2024-03-08T09:15:12","guid":{"rendered":"https:\/\/www.ipsen.com\/switzerland\/?page_id=35"},"modified":"2025-09-17T15:03:29","modified_gmt":"2025-09-17T13:03:29","slug":"seltene-erkrankungen","status":"publish","type":"page","link":"https:\/\/www.ipsen.com\/austria\/seltene-erkrankungen\/","title":{"rendered":"Seltene Erkrankungen"},"content":{"rendered":"    <section class=\"sub-page-banner bg-img-enabled  banner-no-filter\" style=\"background-image:url(https:\/\/www.ipsen.com\/austria\/wp-content\/uploads\/sites\/12\/2025\/07\/Health-Rare-Disease.jpg)\">\n                <div class=\"container content-sec\">\n            <nav aria-label=\"breadcrumb\">\n            <ol class=\"breadcrumb\">\n                <li class=\"breadcrumb-item\"><a href=\"https:\/\/www.ipsen.com\/austria\">Home<\/a><\/li><li class=\"breadcrumb-item active\"><a href=\"#\" aria-current=\"page\">Therapiegebiete &#8211; Seltene Erkrankungen<\/a><\/li><\/ol>\n            <\/nav>            <h1 class=\"visible banner-font-color-white\">Seltene Erkrankungen<\/h1>\n            <p class=\"visible banner-font-color-white\">Entwicklung von Behandlungsm\u00f6glichkeiten f\u00fcr Menschen mit seltenen und sehr seltenen Krankheiten<\/p>\n        <\/div>\n    <\/section>\n\n\n\n<!-- Ipsen Content Overlay Start -->\n<section class=\"two-col-image-section\">\n    <div class=\"container two-img-section-innner\"  >\n        <div class=\"content-overlay-inner bg-color-enabled\" style=\"background-color:#EDEBE4\">\n                <!-- Ipsen Content Overlay Variation Two Start -->\n                <div class=\"row \">\n                    <div class=\"col-xs-12 col-sm-12 col-md-6 column-1 \">\n                        <div id=\"image-carousel\" class=\"img-video-section carousel\" data-bs-ride=\"carousel\">\n                            <div class=\"carousel-inner\">\n                                                                        <div class=\"carousel-item active\">\n                                            <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/austria\/wp-content\/uploads\/sites\/12\/2024\/10\/Gill-PCB-2.jpg\" alt=\"Media Image\" >\n                                        <\/div>\n                                                            <\/div>\n                                                    <\/div>\n                    <\/div>\n                    <div class=\" col-xs-12 col-sm-12 col-md-6 column-2 \">\n                        <div class=\" section-content\">\n                                                                <div class=\"heading-dash\">\n                                        <span class=\"dash\"><\/span>\n                                        <h4 role=\"heading\" aria-level=\"2\" class=\"heading-para-right heading-four\">\n                                            Unser Engagement f\u00fcr seltene Krankheiten                                        <\/h4>\n                                    <\/div>\n                                                                                                                        <p class=\"section-para \">\n                                        F\u00fcr 94 % der seltenen Krankheiten gibt es noch immer keine Behandlung. Wir nutzen unser wissenschaftliches Fachwissen, unsere globale Pr\u00e4senz und eine externe Innovationsstrategie, um lebensver\u00e4ndernde Medikamente f\u00fcr seltene Erkrankungen zu entwickeln.\r\n                                    <\/p>\n                                                                                <\/div>\n                    <\/div>\n                    <!-- Ipsen Content Overlay Variation Two End -->\n                <\/div>\n        <!-- Ipsen Content Overlay Variation two End -->\n                <\/div>\n    <\/div>\n<\/section>\n<!-- Ipsen Content Overlay End -->\n\n<!-- Text & Media Block Code -->\n<section class=\"two-col-section text-media-section\">\n    <div class=\"container two-section-innner section-reverse\">\n        <div class=\"response-inner\" style=\"background-image: url('')\">\n            <div class=\"row section-reverse\">\n                <div class=\"col-xs-12 col-sm-12 col-md-6\">\n                                                    <div class=\"img-video-section\">\n                                <img decoding=\"async\" \n                                    src=\"https:\/\/www.ipsen.com\/austria\/wp-content\/uploads\/sites\/12\/2024\/10\/Gill-PBC-3.jpg\" \n                                    alt=\"\" \n                                >\n                            <\/div>\n                                        <\/div>\n                <div class=\" col-xs-12 col-sm-12 col-md-6\">\n                    <div class=\"section-content\">\n                        <div class=\"heading-dash\">\n                                                            <span class=\"dash\"><\/span>\n                                <h4 class=\"heading-para heading-four\" role=\"heading\" aria-level=\"2\">\n                                    Wir h\u00f6ren Menschen zu, die mit seltenen Erkrankungen leben                                <\/h4>\n                                                    <\/div>\n                                                <p>Auf unserem unerm\u00fcdlichen Weg in der Patientenversorgung bem\u00fchen wir uns, die Herausforderungen zu verstehen, mit denen Menschen mit seltenen Krankheiten leben. Wir lernen von ihren Erfahrungen und integrieren ihre Erkenntnisse in unsere Arbeit w\u00e4hrend des gesamten Entwicklungsprozesses. Dadurch gewinnen wir an Dynamik bei der Entwicklung von Therapien f\u00fcr seltene Krankheiten.<\/p>\n                            <a \n                            aria-label=\" about Wir h\u00f6ren Menschen zu, die mit seltenen Erkrankungen leben\"  \n                                role=\"link\" \n                                class=\"btn-link hidden\"\n                                href=\"\" \n                                target=\"_self\"\n                            > \n                                 \n                            <\/a>\n\n                    <\/div>\n                <\/div>\n            <\/div>\n        <\/div>\n    <\/div>\n<\/section>\n\n<!--Graphics Cards Carousel Start Here-->\n\n    <section class=\"graphic-card graphics-old-layout bg-color-disabled bg-image-disabled bg-video-disabled bg-mobile-video-img-disabled\"    data-displaycards=\"3\">\n                <div class=\"container\">\n            <div class=\"text-graph-inner\">\n                <div class=\"row\">\n                    <!--Graphic info section-->\n                    <div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n                        <div class=\"text-graph-heading\">\n                        <h3 class=\"charcoal-grey visible heading-three\" role=\"heading\" aria-level=\"2\">\n                                Behandlungsparadigmen in Frage stellen                             <\/h3>\n                            <p class=\"text-graph-para charcoal-grey visible\">Ipsen konzentriert sich auf die Entwicklung bahnbrechender Therapien f\u00fcr seltene Krankheiten<\/p>\n                        <\/div>\n                    <\/div><!--Graphic info section over here -->\n\n                    <!--Graphic detail section-->\n                    <div class=\"column-2 col-xl-12 col-md-12 col-sm-12\">\n                        <!-- graphic-card carousel start here -->\n                                                    <div class=\"text-graph-carousel\">\n                                <div class=\"glider-contain multiple\">\n                                                                                    <div class=\"text-graph-content-btn\">\n                                                    <button aria-hidden=\"true\" aria-label=\"Vorherige\" class=\"glider-graphic-card-prev\"><span><\/span><\/button>\n                                                    <button aria-hidden=\"true\" aria-label=\"N\u00e4chstes\" class=\"glider-graphic-card-next\"><span><\/span><\/button>\n                                                <\/div>\n                                    \n                                <div class=\"glider-graphic-card\" tabindex=\"-1\">\n                                                                                                                        <div class=\"text-graphic\">\n                                                    <div class=\"text-graph-row\">\n                                                        \n                                                                <!-- Graphic Card With OLD layout start here -->\n                                                                <div class=\"column-1\">\n                                                                                                                                                <div class=\"text-graph-img visible graphic-icon-enabled \">\n                                                                                                                                                                    <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/austria\/wp-content\/uploads\/sites\/12\/2025\/07\/Portfolio-1.png\" alt=\"\" \/> \n                                                                                                                                                            <\/div>\n                                                                                                                                    <\/div>\n                                                                <div class=\"column-2\">\n                                                                    <div class=\"text-graph-content\">\n                                                                                                                                                        <div class=\"text-graph-title\">\n                                                                                <h4 role=\"heading\" aria-level=\"3\">Einzigartige Herausforderungen erfordern einzigartige L\u00f6sungen <\/h4>\n                                                                                <\/div>\n                                                                                                                                                <div class=\"text-graph-desc\">\n                                                                            <p><p>In den letzten Jahren haben wir unser Portfolio f\u00fcr seltene Krankheiten mit Therapien und Pr\u00fcfpr\u00e4paraten f\u00fcr seltene Lebererkrankungen bei Kindern und Erwachsenen weiter gest\u00e4rkt.<\/p>\n<\/p>\n                                                                        <\/div>\n                                                                    <\/div>\n                                                                <\/div>\n                                                                <!-- Graphic Card With OLD layout end here -->\n                                                        \n                                                    <\/div>\n                                                <\/div>\n                                                                                                                                                                    <div class=\"text-graphic\">\n                                                    <div class=\"text-graph-row\">\n                                                        \n                                                                <!-- Graphic Card With OLD layout start here -->\n                                                                <div class=\"column-1\">\n                                                                                                                                                <div class=\"text-graph-img visible graphic-icon-enabled \">\n                                                                                                                                                                    <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/austria\/wp-content\/uploads\/sites\/12\/2025\/07\/People.png\" alt=\"\" \/> \n                                                                                                                                                            <\/div>\n                                                                                                                                    <\/div>\n                                                                <div class=\"column-2\">\n                                                                    <div class=\"text-graph-content\">\n                                                                                                                                                        <div class=\"text-graph-title\">\n                                                                                <h4 role=\"heading\" aria-level=\"3\">Ein unersch\u00fctterlicher Kampf f\u00fcr die Bed\u00fcrfnisse der Patient:innen<\/h4>\n                                                                                <\/div>\n                                                                                                                                                <div class=\"text-graph-desc\">\n                                                                            <p><p>F\u00fcr 94 % der seltenen Krankheiten gibt es noch keine zugelassenen Behandlungen.<\/p>\n<\/p>\n                                                                        <\/div>\n                                                                    <\/div>\n                                                                <\/div>\n                                                                <!-- Graphic Card With OLD layout end here -->\n                                                        \n                                                    <\/div>\n                                                <\/div>\n                                                                                                                                                                    <div class=\"text-graphic\">\n                                                    <div class=\"text-graph-row\">\n                                                        \n                                                                <!-- Graphic Card With OLD layout start here -->\n                                                                <div class=\"column-1\">\n                                                                                                                                                <div class=\"text-graph-img visible graphic-icon-enabled \">\n                                                                                                                                                                    <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/austria\/wp-content\/uploads\/sites\/12\/2025\/07\/Family.png\" alt=\"\" \/> \n                                                                                                                                                            <\/div>\n                                                                                                                                    <\/div>\n                                                                <div class=\"column-2\">\n                                                                    <div class=\"text-graph-content\">\n                                                                                                                                                        <div class=\"text-graph-title\">\n                                                                                <h4 role=\"heading\" aria-level=\"3\">Selten, aber nicht allein<\/h4>\n                                                                                <\/div>\n                                                                                                                                                <div class=\"text-graph-desc\">\n                                                                            <p><p>350-400 Millionen Menschen sind weltweit von einer der 7 000 seltenen Krankheiten betroffen.<\/p>\n<\/p>\n                                                                        <\/div>\n                                                                    <\/div>\n                                                                <\/div>\n                                                                <!-- Graphic Card With OLD layout end here -->\n                                                        \n                                                    <\/div>\n                                                <\/div>\n                                                                                                                                                                    <div class=\"text-graphic\">\n                                                    <div class=\"text-graph-row\">\n                                                        \n                                                                <!-- Graphic Card With OLD layout start here -->\n                                                                <div class=\"column-1\">\n                                                                                                                                                <div class=\"text-graph-img visible graphic-icon-enabled \">\n                                                                                                                                                                    <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/austria\/wp-content\/uploads\/sites\/12\/2025\/07\/Clinical-Studies.png\" alt=\"\" \/> \n                                                                                                                                                            <\/div>\n                                                                                                                                    <\/div>\n                                                                <div class=\"column-2\">\n                                                                    <div class=\"text-graph-content\">\n                                                                                                                                                        <div class=\"text-graph-title\">\n                                                                                <h4 role=\"heading\" aria-level=\"3\">Innovationen f\u00fcr Patient:innen mit seltenen Krankheiten <\/h4>\n                                                                                <\/div>\n                                                                                                                                                <div class=\"text-graph-desc\">\n                                                                            <p><p>Unsere klinische Pipeline f\u00fcr seltene Krankheiten hat sich seit 2020 mehr als verdoppelt.<\/p>\n<\/p>\n                                                                        <\/div>\n                                                                    <\/div>\n                                                                <\/div>\n                                                                <!-- Graphic Card With OLD layout end here -->\n                                                        \n                                                    <\/div>\n                                                <\/div>\n                                                                                                                <\/div>\n                            <\/div>\n                                            <\/div> <!-- graphic-card carousel end here -->\n                <\/div> <!--Graphic detail section over here with 12 grid -->   \n            <\/div><!--row ended here-->\n        <\/div> <!-- graph-inner ended here -->\n        \n            <div class=\"more-result-btn\">\n                                            <\/div>\n        <\/div> <!--Container class ended here -->\n    <\/section>\n<!--Graphics Cards Carousel End Here-->\n\n\n    <section class=\"title-text \">\n        <div class=\"container\">\n            <div class=\"title-text-inner\" style=\"background-color:#EDEBE4;\">\n\n                <!-- If heading is enabled then it's visible -->\n                <div class=\"text-head-dash visible\">\n                <h3 class=\"heading-three\" role=\"heading\" aria-level=\"2\">\n                        Kontinuierliche Pionierarbeit bei seltenen Krankheiten                    <\/h3>\n                <\/div>\n               \n                <!-- If description is enabled then it's visible -->\n                <div class=\"text-parbase visible\">\n                    <p>Als Kernst\u00fcck unserer Strategie konzentriert sich Ipsen seit vielen Jahren auf die Entwicklung bahnbrechender Therapien f\u00fcr seltene Krankheiten.<\/p>\n                <\/div>\n\n                <!-- If button is enabled then it's visible -->\n                \n            <\/div>\n        <\/div>\n    <\/section>\n\n\n\n    <!--Accordion Cards Start Here-->\n    <section class=\"accordion bg-color-disabled\"  data-according-id=\"1036552395\">\n        <div class=\"container\">\n            <div class=\"row\">\n                <!--Accordion info section-->\n                <div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n                    <div class=\"accordian-info\">\n                        <h3 class=\"accordian-heading visible heading-three\" role=\"heading\" aria-level=\"2\">\n                            Seltene Leberkrankheiten                        <\/h3>\n                        <p class=\"accordian-summary hidden\"><\/p>\n                    <\/div>\n                <\/div><!--Accordion info section over here -->\n\n                <div class=\"col-xl-12 col-lg-12 col-md-12 col-sm-12\">\n                    <div class=\"accordion accor-group\" id=\"accordionExample1036552395\">\n                         \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading0\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading10365523950\" aria-expanded=\"false\" aria-controls=\"expHeading10365523950\">\n                                                 Progressive famili\u00e4re intrahepatische Cholestase (PFIC)                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading10365523950\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading0\" data-bs-parent=\"#accordionExample1036552395\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><p>Die progressive famili\u00e4re intrahepatische Cholestase (PFIC) ist eine seltene und potenziell lebensbedrohliche Lebererkrankung bei Kindern. Gallens\u00e4ure kann aus der Leber nicht abgeleitet werden und sammelt sich in den Leberzellen an (Cholestase). Dies verursacht Lebersch\u00e4den und Symptome. Betroffene Patient*innen leiden unter qu\u00e4lendem Juckreiz, der die Lebensqualit\u00e4t deutlich einschr\u00e4nkt und zu Schlaflosigkeit, Reizbarkeit und schlechter Aufmerksamkeit f\u00fchrt. PFIC kann im Verlauf zu Leberzirrhose und Leberversagen f\u00fchren, wodurch eine Organtransplantation notwendig werden kann. PFIC tritt bei ca. 1 von 100 000 Lebendgeburten auf und wird vererbt.<\/p>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                             \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading1\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading10365523951\" aria-expanded=\"false\" aria-controls=\"expHeading10365523951\">\n                                                Prim\u00e4r bili\u00e4re Cholangitis (PBC)                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading10365523951\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading1\" data-bs-parent=\"#accordionExample1036552395\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><p>Die prim\u00e4r bili\u00e4re Cholangitis (PBC, fr\u00fchere Bezeichnung: prim\u00e4r bili\u00e4re Zirrhose, PBZ) ist eine seltene chronische Erkrankung, bei der die Galleng\u00e4nge in der Leber langsam zerst\u00f6rt werden. Wenn die Galleng\u00e4nge gesch\u00e4digt sind, k\u00f6nnen sich Gallens\u00e4uren in der Leber stauen und zu einer irreversiblen Vernarbung des Lebergewebes (Zirrhose) f\u00fchren. Im Fr\u00fchstadium bleibt die Krankheit h\u00e4ufig unentdeckt und verursacht unspezifische Symptome wie M\u00fcdigkeit oder Bauchschmerzen. Einige Patient*innen leiden jedoch unter starkem Juckreiz. PBC tritt bei ca. 1-2 von 100 000 Einwohner*innen und zu 90% bei Frauen auf.<\/p>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                             \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading2\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading10365523952\" aria-expanded=\"false\" aria-controls=\"expHeading10365523952\">\n                                                Alagille-Syndrom (ALGS)                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading10365523952\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading2\" data-bs-parent=\"#accordionExample1036552395\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><p>Das Alagille-Syndrom (ALGS) ist eine seltene, genetisch bedingte Erkrankung, die verschiedene Organsysteme wie Leber, Herz, Skelett, Augen, zentrales Nervensystem, Blutgef\u00e4sse und Knochen betreffen kann. Etwa 90 % der Personen mit ALGS zeigen Anomalien in den Galleng\u00e4ngen innerhalb der Leber (Gallengangshypoplasie), was zu einem R\u00fcckstau von Gallens\u00e4uren in der Leber (Cholestase) f\u00fchren kann. Dies wiederum verursacht eine fortschreitende Lebererkrankung. Betroffene leiden oft unter Symptomen wie starkem Juckreiz und Gelbf\u00e4rbung der Haut.<\/p>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                                                <\/div>\n                <\/div> \n            <\/div>\n        <\/div>\n    <\/section>\n    <!--Accordion Cards End Here-->\n\n\n\n    <!--Accordion Cards Start Here-->\n    <section class=\"accordion bg-color-disabled\"  data-according-id=\"1707505651\">\n        <div class=\"container\">\n            <div class=\"row\">\n                <!--Accordion info section-->\n                <div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n                    <div class=\"accordian-info\">\n                        <h3 class=\"accordian-heading visible heading-three\" role=\"heading\" aria-level=\"2\">\n                            Wachstumsst\u00f6rungen                        <\/h3>\n                        <p class=\"accordian-summary hidden\"><\/p>\n                    <\/div>\n                <\/div><!--Accordion info section over here -->\n\n                <div class=\"col-xl-12 col-lg-12 col-md-12 col-sm-12\">\n                    <div class=\"accordion accor-group\" id=\"accordionExample1707505651\">\n                         \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading0\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading17075056510\" aria-expanded=\"false\" aria-controls=\"expHeading17075056510\">\n                                                Akromegalie                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading17075056510\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading0\" data-bs-parent=\"#accordionExample1707505651\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><p>Akromegalie ist eine seltene Erkrankung, die durch einen gutartigen Tumor (Adenom) in der Hirnanhangsdr\u00fcse (Hypophyse) verursacht wird. Dieser Tumor f\u00fchrt zu einer \u00fcberm\u00e4ssigen Freisetzung von Wachstumshormon (GH) in den Blutkreislauf, was zu einem unkontrollierten Wachstum von Gewebe und Organen im K\u00f6rper, insbesondere von Knochen, Knorpel und anderen Geweben f\u00fchrt. Typische Anzeichen sind vergr\u00f6sserte H\u00e4nde, F\u00fcsse und Ver\u00e4nderung der Gesichtsz\u00fcge wie eine verbreiterte Nase und ein vergr\u00f6sserter Kiefer (Gigantismus). Es erkranken pro Jahr ca. 3-4 pro 1 000 000 Einwohner*innen an Akromegalie, am h\u00e4ufigsten zwischen dem 40. und 50. Lebensjahr.<\/p>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                             \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading1\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading17075056511\" aria-expanded=\"false\" aria-controls=\"expHeading17075056511\">\n                                                Schwerer prim\u00e4rer Mangel an IGF-1                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading17075056511\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading1\" data-bs-parent=\"#accordionExample1707505651\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n<div class=\"accordian-info\">\n<p class=\"accordian-summary visible\">Ein schwerer prim\u00e4rer Mangel an IGF-1 (<em>insulin like groth factor 1<\/em>; dieses Protein vermittelt die Wirkungen des Wachstumshormons) f\u00fchrt bei Kindern und Jugendlichen zu Wachstumsst\u00f6rungen sowie zu verschiedenen anatomischen, morphologischen und physiologischen Beeintr\u00e4chtigungen.<\/p>\n<\/div>\n<\/div>\n<div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n<div class=\"accordian-info\">\n<p>In der Praxis trifft die Bezeichnung schwerer prim\u00e4rer IGF-Mangel auf Kinder zu, die folgende Symptome aufweisen:<\/p>\n<\/div>\n<\/div>\n<ul>\n<li>Geringe K\u00f6rpergr\u00f6\u00dfe<\/li>\n<li>Basale IGF-1-Konzentration gering (altersangepasst)<\/li>\n<li>Basale GH-Konzentration normal oder hoch<\/li>\n<\/ul>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                                                <\/div>\n                <\/div> \n            <\/div>\n        <\/div>\n    <\/section>\n    <!--Accordion Cards End Here-->\n\n\n\n    <!--Accordion Cards Start Here-->\n    <section class=\"accordion bg-color-disabled\"  data-according-id=\"28967139\">\n        <div class=\"container\">\n            <div class=\"row\">\n                <!--Accordion info section-->\n                <div class=\"column-1 col-xl-12 col-md-12 col-sm-12\">\n                    <div class=\"accordian-info\">\n                        <h3 class=\"accordian-heading visible heading-three\" role=\"heading\" aria-level=\"2\">\n                            Knochenerkrankungen                        <\/h3>\n                        <p class=\"accordian-summary hidden\"><\/p>\n                    <\/div>\n                <\/div><!--Accordion info section over here -->\n\n                <div class=\"col-xl-12 col-lg-12 col-md-12 col-sm-12\">\n                    <div class=\"accordion accor-group\" id=\"accordionExample28967139\">\n                         \n                                    <!-- Accordion with Expandable panel & FAQs -->\n                                    <div class=\"accordion-item accor-item\">\n                                        <p  role=\"heading\" aria-level=\"3\" class=\"accordion-header accor-head-para\" id=\"expHeading0\">\n                                            <button class=\"accordion-button accor-btn collapsed\" type=\"button\" data-bs-toggle=\"collapse\" data-bs-target=\"#expHeading289671390\" aria-expanded=\"false\" aria-controls=\"expHeading289671390\">\n                                                Fibrodysplasia ossificans progressiva (FOP)                                            <\/button>\n                                        <\/p>\n                                        <div id=\"expHeading289671390\" class=\"accordion-collapse collapse \" aria-labelledby=\"expHeading0\" data-bs-parent=\"#accordionExample28967139\">\n                                            <div class=\"accordion-body\">\n                                                <div class=\"accordion-data\">\n                                                    <p><p>FOP verursacht eine dauerhafte und kontinuierliche abnorme Knochenneubildung in Weich- und Bindegeweben wie Muskeln, Sehnen und B\u00e4ndern. Dieser Prozess ist als heterotope Ossifikation (HO) bekannt. Es handelt sich um eine \u00e4u\u00dferst seltene genetische St\u00f6rung, die durch Entz\u00fcndungssch\u00fcbe, die zu abnormer Knochenbildung f\u00fchren, gekennzeichnet ist, die in der Kindheit beginnen. HO ist irreversibel und f\u00fchrt zu schweren funktionellen Einschr\u00e4nkungen der Mobilit\u00e4t, fortschreitender und kumulativer Behinderung und verk\u00fcrzter Lebenserwartung. Im Durchschnitt wird die Krankheit im Alter von 5 Jahren diagnostiziert und die durchschnittliche Lebenserwartung liegt bei 56 Jahren. Weltweit leben derzeit etwa 900 Menschen mit einer FOP-Diagnose.<\/p>\n<\/p>\n                                                    <div class=\"cta-block hidden\" >\n                                                                                                            <\/div>\n                                                <\/div>\n                                            <\/div>\n                                        <\/div>\n                                    <\/div>\n                                                <\/div>\n                <\/div> \n            <\/div>\n        <\/div>\n    <\/section>\n    <!--Accordion Cards End Here-->\n\n\n<!-- Ipsen Content Overlay Start -->\n<section class=\"two-col-image-section\">\n    <div class=\"container two-img-section-innner\"  >\n        <div class=\"content-overlay-inner bg-color-enabled\" style=\"background-color:#EDEBE4\">\n                <!-- Ipsen Content Overlay Variation Two Start -->\n                <div class=\"row \">\n                    <div class=\"col-xs-12 col-sm-12 col-md-6 column-1 \">\n                        <div id=\"image-carousel\" class=\"img-video-section carousel\" data-bs-ride=\"carousel\">\n                            <div class=\"carousel-inner\">\n                                                                        <div class=\"carousel-item active\">\n                                            <img decoding=\"async\" src=\"https:\/\/www.ipsen.com\/austria\/wp-content\/uploads\/sites\/12\/2025\/07\/Module-2-\u2013-Brief-about-neuroscience_IPSEN_Production_Signes_060.jpg\" alt=\"Media Image\" >\n                                        <\/div>\n                                                            <\/div>\n                                                    <\/div>\n                    <\/div>\n                    <div class=\" col-xs-12 col-sm-12 col-md-6 column-2 \">\n                        <div class=\" section-content\">\n                                                                <div class=\"heading-dash\">\n                                        <span class=\"dash\"><\/span>\n                                        <h4 role=\"heading\" aria-level=\"2\" class=\"heading-para-right heading-four\">\n                                            Klinische Studien bei seltenen Erkrankungen                                        <\/h4>\n                                    <\/div>\n                                                                                                                        <p class=\"section-para \">\n                                        Wir arbeiten fortlaufend daran, neue Therapien in die klinische Forschung zu bringen um seltene Erkrankungen zu behandeln, f\u00fcr welche Patient*innen bisher keine oder nur wenige Optionen haben.                                    <\/p>\n                                                                                                <a \n                                            role=\"link\" \n                                            class=\"btn-link section-btn cta-visible\" \n                                            href=\"https:\/\/www.ipsen.com\/clinical-trials\/find-a-clinical-trial\/\" \n                                            aria-label=\"\" \n                                            target=\"_blank\"\n                                        >\n                                            Ipsen Studien-Finder                                        <\/a>    \n                                    <\/button>\n                                                    <\/div>\n                    <\/div>\n                    <!-- Ipsen Content Overlay Variation Two End -->\n                <\/div>\n        <!-- Ipsen Content Overlay Variation two End -->\n                <\/div>\n    <\/div>\n<\/section>\n<!-- Ipsen Content Overlay End -->\n\n\n<p class=\"has-text-align-center has-small-font-size\">ALLSC-AT-000037, 01\/2025<\/p>\n","protected":false},"excerpt":{"rendered":"","protected":false},"author":2,"featured_media":0,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_acf_changed":false,"footnotes":""},"class_list":["post-43","page","type-page","status-publish","hentry","entry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v26.8 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>Pionierarbeit bei der Behandlung seltener Krankheiten<\/title>\n<meta name=\"description\" content=\"Ipsen widmet sich der Entwicklung innovativer Medikamente f\u00fcr seltene Krankheiten und konzentriert sich dabei auf drei Hauptbereiche: Knochen- und endokrine Erkrankungen, neuromuskul\u00e4re Erkrankungen und Lebererkrankungen.\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" 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